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Medical Condition

huntington disease

Total Trials
9
Recruiting Now
9
Trial Phases
Phase 2

ClinicalMetric tracks all active clinical trials for huntington disease sourced from ClinicalTrials.gov. Research in this area spans early-phase safety investigations through large Phase 3 confirmatory trials, conducted by NIH-funded academic centers, independent investigators, and pharmaceutical sponsors worldwide. Each listing is updated daily as new studies open enrollment and existing ones reach capacity or complete follow-up.

Trial listings include the NCT identifier, current recruitment status, phase classification, primary and secondary endpoints, estimated enrollment size, participating countries, and direct links to the full protocol on ClinicalTrials.gov. Eligibility criteria — including age range, disease stage, and prior treatment requirements — are documented for every study to help patients and clinicians assess suitability before contacting a trial site.

Frequently Asked Questions — huntington disease Clinical Trials

How many clinical trials are currently recruiting for huntington disease?
ClinicalMetric currently tracks 9 actively recruiting clinical trials for huntington disease, sourced in real time from ClinicalTrials.gov. The total number of registered studies—including those not yet enrolling or in active follow-up—is 9. Trial availability changes daily as new studies open enrollment and existing ones reach capacity.
What trial phases are available for huntington disease?
huntington disease research spans Phase 2 (3 trials). Phase 1 studies evaluate safety and dosing in small groups, Phase 2 studies assess preliminary efficacy in 100–300 participants, and Phase 3 trials compare the new treatment against the standard of care in 300–3,000+ patients. Phase 4 post-approval studies monitor long-term outcomes in real-world populations.
How do I find out if I qualify for a huntington disease clinical trial?
Eligibility criteria for huntington disease trials vary by study and typically specify age range, disease stage or severity, prior treatment history, and specific diagnostic or laboratory parameters. Each listing on ClinicalMetric links to the full protocol on ClinicalTrials.gov, where inclusion and exclusion criteria are documented. Contact the sponsoring site's research coordinator directly to confirm your eligibility—your treating physician or specialist can also help identify the most appropriate trial based on your medical history and current treatment status.
Trial Phases
Phase 2
3
Top Sponsors
University of Rochester 1 trial
University Hospital, Grenoble 1 trial
Oslo University Hospital 1 trial
Fundación Pública Andaluza para la gestión de la Investigación en Sevilla 1 trial
Western Sydney Local Health District 1 trial

Recruiting Clinical Trials

NCT07010705
Recruiting
Digital Measures for Clinical Trial Endpoints in Huntington's Disease
Enrollment
100 pts
Location
United States
Sponsor
University of Rochester
View Trial →
NCT06626308
Recruiting
Early Biomarkers in Premanifest Huntington's Disease Gene Carriers: a Pilot Study
Enrollment
20 pts
Location
France
Sponsor
University Hospital, Grenoble
View Trial →
NCT06853743 Phase 2
Recruiting
The NAD-HD Study: A Study to Investigate Efficacy and Safety of Nicotinamide Riboside Compared With Placebo in Huntington's Disease
Enrollment
120 pts
Location
Norway
Sponsor
Oslo University Hospital
View Trial →
NCT04478734 Phase 2
Recruiting
Trial of the Combined Use of Thiamine and Biotin in Patients With Huntington's Disease
Enrollment
24 pts
Location
Spain
Sponsor
Fundación Pública Andaluza par...
View Trial →
NCT05509153 Phase 2
Recruiting
A Randomised Controlled Trial, Of N-Acetyl Cysteine (NAC), for Premanifest Huntingtin Gene Expansion Carriers
Enrollment
160 pts
Location
Australia
Sponsor
Western Sydney Local Health Di...
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NCT02994719
Recruiting
Gait Analysis in Neurological Disease
Enrollment
120 pts
Location
United States
Sponsor
Beth Israel Deaconess Medical ...
View Trial →
NCT06203106
Recruiting
NYSCF Scientific Discovery Biobank
Enrollment
10,000 pts
Location
United States
Sponsor
New York Stem Cell Foundation ...
View Trial →
NCT07213648
Recruiting
Modification of Threat Interpretation Bias to Reduce Anxiety in Neurodegenerative Movement Disorders (Aim 3)
Enrollment
136 pts
Location
United States
Sponsor
University of Virginia
View Trial →
NCT06539169
Recruiting
FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases
Enrollment
1,000 pts
Location
United States
Sponsor
xCures
View Trial →

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ClinicalMetric — Independent clinical trial intelligence platform. Not affiliated with NIH, ClinicalTrials.gov, the U.S. FDA, or any pharmaceutical company, hospital, or clinical research organization. Trial data is sourced from ClinicalTrials.gov for informational purposes only and does not constitute medical advice. Do not make any treatment, enrollment, or health decisions based solely on information found here — always consult a qualified healthcare professional. Full Disclaimer  ·  Last Reviewed: April 2026  ·  Data Methodology