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RecruitingNCT05554835

Global Registry and Natural History Study for Mitochondrial Disorders

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Plain-language summary for patients

Trial Parameters

ConditionMitochondrial Diseases
SponsorLMU Klinikum
Study TypeOBSERVATIONAL
PhaseN/A
Enrollment6,000
SexALL
Min AgeN/A
Max AgeN/A
Start Date2009-02-01
Completion2040-12

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Brief Summary

The main goal of the project is provision of a global registry for mitochondrial disorders to harmonize previous national registries, enable world-wide participation and facilitate natural history studies, definition of outcome measures and conduction of clinical trials.

Eligibility Criteria

Inclusion Criteria: * suspected or confirmed mitochondrial disease * willingness to participate Exclusion Criteria: * unwillingness to participate

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