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Medical Condition
mitochondrial diseases
Total Trials
4
Recruiting Now
4
Trial Phases
Phase 3, Phase 2
NCT06451757 Phase 3
Recruiting
KHENERFIN Study: A Trial to Evaluate the Efficacy and Safety of Sonlicromanol in Primary Mitochondrial Diseases
Enrollment
220 pts
Location
United States, Denma...
Sponsor
Khondrion BV
NCT06017869 Phase 2
Recruiting
Evaluate the Safety and Therapeutic Effects of a Single Intravenous Infusion (IV) of Autologous CD34+ Cells Enriched With Allogenic Placenta-derived Mitochondria in Patients With a Diagnosis of Pearson Syndrome (PS)
Enrollment
6 pts
Location
Israel
Sponsor
Minovia Therapeutics Ltd.
NCT01793168
Recruiting
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Enrollment
20,000 pts
Location
United States, Austr...
Sponsor
Sanford Health
NCT01694940
Recruiting
North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
Enrollment
1,000 pts
Location
United States, Canad...
Sponsor
Columbia University