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Recruiting NCT01873924

NCT01873924 Clinical and Neuropsychological Investigations in Batten Disease

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Clinical Trial Summary
NCT ID NCT01873924
Status Recruiting
Phase
Sponsor University of Rochester
Condition Neuronal Ceroid Lipofuscinosis
Study Type OBSERVATIONAL
Enrollment 500 participants
Start Date 2004-08
Primary Completion 2035-08

Eligibility & Interventions

Sex All sexes
Min Age N/A
Max Age N/A
Study Type OBSERVATIONAL

Eligibility Fast-Check

Enter your details for a quick preliminary check. This does not replace medical advice.

What to Expect as a Participant

This is an observational study. You will not receive an experimental treatment; researchers will collect data based on your existing condition or standard treatment.

This trial targets 500 participants in total. It began in 2004-08 with a primary completion date of 2035-08.

⚠ This information is for research awareness only. Always consult your physician before joining any clinical trial. Participation is voluntary and you may withdraw at any time.

Brief Summary

This study aims to assess the natural history of Batten disease (Neuronal Ceroid Lipofuscinosis) by obtaining information about the motor, behavioral, and functional capabilities of individuals with Batten disease. This study will also refine and validate the Unified Batten Disease Rating Scale (UBDRS) as a clinical rating instrument for Batten disease.

Eligibility Criteria

Inclusion Criteria: * child or adult with any form of Batten disease * parent or legal guardian of a child or adult with any form of Batten disease Exclusion Criteria: \- parent or guardian unable or unwilling to provide permission for the affected individual

Contact & Investigator

Central Contact

Amy Vierhile, RN PNP

✉ amy_vierhile@urmc.rochester.edu

📞 (585)275-4762

Principal Investigator

Jonathan W Mink, MD PhD

PRINCIPAL INVESTIGATOR

University of Rochester

Frequently Asked Questions

Who can join the NCT01873924 clinical trial?

This trial is open to participants of all sexes, studying Neuronal Ceroid Lipofuscinosis. Full inclusion and exclusion criteria are listed in the Eligibility Criteria section. Always confirm your eligibility with the research team before applying.

Is NCT01873924 currently recruiting?

Yes, NCT01873924 is actively recruiting participants. Contact the research team at amy_vierhile@urmc.rochester.edu for enrollment information.

Where is the NCT01873924 trial being conducted?

This trial is being conducted at Rochester, United States.

Who is sponsoring the NCT01873924 clinical trial?

NCT01873924 is sponsored by University of Rochester. The principal investigator is Jonathan W Mink, MD PhD at University of Rochester. The trial plans to enroll 500 participants.

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