← Browse by Condition
Medical Condition
batten disease
Total Trials
2
Recruiting Now
2
Trial Phases
Phase 1
NCT04613089
Recruiting
Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD Database
Enrollment
500 pts
Location
Germany
Sponsor
Universitätsklinikum Hamburg-E...
NCT02254863 Phase 1
Recruiting
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
Enrollment
40 pts
Location
United States
Sponsor
Joanne Kurtzberg, MD