SPONSOR
Vertex Pharmaceuticals Incorporated
Total Trials
3
Recruiting
3
Phases
Phase 1, Phase 3
Conditions studied: Cystic FibrosisBeta-ThalassemiaThalassemiaHematologic DiseasesGenetic Diseases, InbornHemoglobinopathiesSickle Cell DiseaseSickle Cell AnemiaNarcolepsy Type 1 (NT1)
Vertex Pharmaceuticals Incorporated is a clinical research sponsor with 3 registered studies on ClinicalTrials.gov, of which 3 are actively recruiting participants. Research covers conditions including Cystic Fibrosis, Beta-Thalassemia, Thalassemia, Hematologic Diseases.
The trial portfolio spans Phase 1, Phase 3 studies, reflecting a pipeline that may include early-stage safety evaluations, mid-stage efficacy assessments, and large-scale confirmatory trials. All studies listed here are sourced directly from ClinicalTrials.gov and updated daily.
Frequently Asked Questions — Vertex Pharmaceuticals Incorporated
How many clinical trials has Vertex Pharmaceuticals Incorporated sponsored?
ClinicalMetric currently tracks 3 clinical trials sponsored by Vertex Pharmaceuticals Incorporated, of which 3 are actively recruiting participants. These trials cover conditions including Cystic Fibrosis, Beta-Thalassemia, Thalassemia. Trial counts are updated daily from ClinicalTrials.gov and reflect currently registered studies.
What therapeutic areas does Vertex Pharmaceuticals Incorporated research focus on?
Vertex Pharmaceuticals Incorporated clinical trials span Cystic Fibrosis, Beta-Thalassemia, Thalassemia, Hematologic Diseases, Genetic Diseases, Inborn, and additional conditions. The research pipeline includes Phase 1, Phase 3 trials, reflecting work from early-stage safety evaluation through large-scale efficacy studies.
How do I participate in a Vertex Pharmaceuticals Incorporated clinical trial?
To participate in a Vertex Pharmaceuticals Incorporated trial, review the active studies listed on this page, check each trial's specific eligibility criteria on ClinicalTrials.gov, and contact the trial site directly—not the sponsor's headquarters. Trial sites are academic medical centers, hospitals, or specialized research clinics. Your physician can facilitate a referral. ClinicalMetric lists all Vertex Pharmaceuticals Incorporated trials with current recruitment status updated daily.
Clinical Trials by Vertex Pharmaceuticals Incorporated
NCT07283770 Phase 1
Recruiting
Dose Escalation Study Evaluating the Safety and Pharmacokinetics of VX-581 in Healthy Participants
Cystic Fibrosis
NCT05477563 Phase 3
Recruiting
Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
Beta-Thalassemia
NCT07584434 Phase 1
Recruiting
A Phase 1, First-in-human Study of VX-433
Narcolepsy Type 1 (NT1)
ClinicalMetric — Independent clinical trial intelligence platform. Not affiliated with NIH, ClinicalTrials.gov, the U.S. FDA, or any pharmaceutical company, hospital, or clinical research organization. Trial data is sourced from ClinicalTrials.gov for informational purposes only and does not constitute medical advice. Do not make any treatment, enrollment, or health decisions based solely on information found here — always consult a qualified healthcare professional. Full Disclaimer · Last Reviewed: April 2026 · Data Methodology