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cystic fibrosis

Total Trials
17
Recruiting Now
17
Trial Phases
Phase 1, Phase 2, Phase 3, Phase 1

ClinicalMetric tracks all active clinical trials for cystic fibrosis sourced from ClinicalTrials.gov. Research in this area spans early-phase safety investigations through large Phase 3 confirmatory trials, conducted by NIH-funded academic centers, independent investigators, and pharmaceutical sponsors worldwide. Each listing is updated daily as new studies open enrollment and existing ones reach capacity or complete follow-up.

Trial listings include the NCT identifier, current recruitment status, phase classification, primary and secondary endpoints, estimated enrollment size, participating countries, and direct links to the full protocol on ClinicalTrials.gov. Eligibility criteria — including age range, disease stage, and prior treatment requirements — are documented for every study to help patients and clinicians assess suitability before contacting a trial site.

Frequently Asked Questions — cystic fibrosis Clinical Trials

How many clinical trials are currently recruiting for cystic fibrosis?
ClinicalMetric currently tracks 17 actively recruiting clinical trials for cystic fibrosis, sourced in real time from ClinicalTrials.gov. The total number of registered studies—including those not yet enrolling or in active follow-up—is 17. Trial availability changes daily as new studies open enrollment and existing ones reach capacity.
What trial phases are available for cystic fibrosis?
cystic fibrosis research spans Phase 1 (3 trials), Phase 2 (2 trials), Phase 3 (1 trial), Phase 4 (1 trial). Phase 1 studies evaluate safety and dosing in small groups, Phase 2 studies assess preliminary efficacy in 100–300 participants, and Phase 3 trials compare the new treatment against the standard of care in 300–3,000+ patients. Phase 4 post-approval studies monitor long-term outcomes in real-world populations.
How do I find out if I qualify for a cystic fibrosis clinical trial?
Eligibility criteria for cystic fibrosis trials vary by study and typically specify age range, disease stage or severity, prior treatment history, and specific diagnostic or laboratory parameters. Each listing on ClinicalMetric links to the full protocol on ClinicalTrials.gov, where inclusion and exclusion criteria are documented. Contact the sponsoring site's research coordinator directly to confirm your eligibility—your treating physician or specialist can also help identify the most appropriate trial based on your medical history and current treatment status.
Trial Phases
Phase 1
3
Phase 2
2
Phase 3
1
Phase 4
1
Top Sponsors
University of California, Los Angeles 2 trials
Charite University, Berlin, Germany 1 trial
Spirovant Sciences, Inc. 1 trial
Indiana University 1 trial
Medical College of Wisconsin 1 trial

Recruiting Clinical Trials

NCT04732910
Recruiting
Modulate-CF: Cystic Fibrosis Transmembrane Regulator (CFTR) Biomarker Study to Evaluate the Rescue of Mutant CFTR in Patients With Cystic Fibrosis Treated With CFTR-modulators
Enrollment
500 pts
Location
Germany
Sponsor
Charite University, Berlin, Ge...
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NCT06526923 Phase 1, Phase 2
Recruiting
A Phase 1/2 Trial of SP-101 for the Treatment of Cystic Fibrosis (CF)
Enrollment
15 pts
Location
United States
Sponsor
Spirovant Sciences, Inc.
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NCT06512064
Recruiting
Acoustic Waveform Respiratory Evaluation
Enrollment
800 pts
Location
United States
Sponsor
Indiana University
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NCT06560463
Recruiting
Continuous Glucose Monitoring and OGTT Screen for Cystic Fibrosis Related Diabetes in Cystic Fibrosis
Enrollment
30 pts
Location
United States
Sponsor
Medical College of Wisconsin
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NCT06810167 Phase 3
Recruiting
Assessing Tenapanor as a Treatment of CF-related Constipation.
Enrollment
25 pts
Location
United States
Sponsor
Massachusetts General Hospital
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NCT06045702
Recruiting
Establishment of a Primary Epididymal Cell Model From Epididymal Samples to Study CFTR Gene Regulation
Enrollment
20 pts
Location
France
Sponsor
University Hospital, Brest
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NCT07283770 Phase 1
Recruiting
Dose Escalation Study Evaluating the Safety and Pharmacokinetics of VX-581 in Healthy Participants
Enrollment
128 pts
Location
United States
Sponsor
Vertex Pharmaceuticals Incorpo...
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NCT06599892
Recruiting
CF Organization of Care in the Era of Highly Effective Modulator.
Enrollment
5,000 pts
Location
France
Sponsor
Hospices Civils de Lyon
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NCT00943514
Recruiting
Natural History of Bronchiectasis
Enrollment
900 pts
Location
United States
Sponsor
National Heart, Lung, and Bloo...
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NCT04469439
Recruiting
Impact of Sinus Surgery on Individuals With Cystic Fibrosis
Enrollment
170 pts
Location
United States
Sponsor
University of California, Los ...
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NCT06836453
Recruiting
Evaluation of New Device for Beta-adrenergic Sweat Test in the Context of Stratification of Patient With Cystic Fibrosis
Enrollment
150 pts
Location
Belgium
Sponsor
Cliniques universitaires Saint...
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NCT06057714
Recruiting
Quantitation and Spatial Registration of Airways Dysfunction With Dynamic 19F MRI in Cystic Fibrosis
Enrollment
30 pts
Location
United States
Sponsor
University of North Carolina, ...
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NCT04509050
Recruiting
Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young Children
Enrollment
210 pts
Location
United States
Sponsor
Sonya Heltshe
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NCT05704036 Phase 4
Recruiting
Estrogen Supplementation and Bone Health in Women With CF
Enrollment
75 pts
Location
United States
Sponsor
Johns Hopkins University
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NCT06191640
Recruiting
Sinus Disease in Young Children With Cystic Fibrosis
Enrollment
80 pts
Location
United States
Sponsor
University of California, Los ...
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NCT06339593 EARLY_Phase 1
Recruiting
Regional Monitoring of CF Lung Disease
Enrollment
60 pts
Location
United States
Sponsor
Children's Hospital Medical Ce...
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NCT02740868 Phase 2
Recruiting
Xenon-129 and Inert Fluorinated Gas Lung MRI: Study of Healthy Volunteers and Participants With Pulmonary Disease
Enrollment
30 pts
Location
Canada
Sponsor
The Hospital for Sick Children
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Related Conditions

asthma (2) bronchiectasis (2) chronic rhinosinusitis diagnosis (2) copd (1) ciliary motility disorders (1) airway malacia (1) healthy control (1) cystic fibrosis related diabetes (1) constipation (1) congenital bilateral absence of vas deferens (1) sterility male (1) autoimmune disease (1)
ClinicalMetric — Independent clinical trial intelligence platform. Not affiliated with NIH, ClinicalTrials.gov, the U.S. FDA, or any pharmaceutical company, hospital, or clinical research organization. Trial data is sourced from ClinicalTrials.gov for informational purposes only and does not constitute medical advice. Do not make any treatment, enrollment, or health decisions based solely on information found here — always consult a qualified healthcare professional. Full Disclaimer  ·  Last Reviewed: April 2026  ·  Data Methodology