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cystic fibrosis

Total Trials
14
Recruiting Now
14
Trial Phases
Phase 2, Phase 1

ClinicalMetric tracks all active clinical trials for cystic fibrosis sourced from ClinicalTrials.gov. Research in this area spans early-phase safety investigations through large Phase 3 confirmatory trials, conducted by NIH-funded academic centers, independent investigators, and pharmaceutical sponsors worldwide. Each listing is updated daily as new studies open enrollment and existing ones reach capacity or complete follow-up.

Trial listings include the NCT identifier, current recruitment status, phase classification, primary and secondary endpoints, estimated enrollment size, participating countries, and direct links to the full protocol on ClinicalTrials.gov. Eligibility criteria — including age range, disease stage, and prior treatment requirements — are documented for every study to help patients and clinicians assess suitability before contacting a trial site.

Frequently Asked Questions — cystic fibrosis Clinical Trials

How many clinical trials are currently recruiting for cystic fibrosis?
ClinicalMetric currently tracks 14 actively recruiting clinical trials for cystic fibrosis, sourced in real time from ClinicalTrials.gov. The total number of registered studies—including those not yet enrolling or in active follow-up—is 14. Trial availability changes daily as new studies open enrollment and existing ones reach capacity.
What trial phases are available for cystic fibrosis?
cystic fibrosis research spans Phase 1 (4 trials), Phase 2 (2 trials). Phase 1 studies evaluate safety and dosing in small groups, Phase 2 studies assess preliminary efficacy in 100–300 participants, and Phase 3 trials compare the new treatment against the standard of care in 300–3,000+ patients. Phase 4 post-approval studies monitor long-term outcomes in real-world populations.
How do I find out if I qualify for a cystic fibrosis clinical trial?
Eligibility criteria for cystic fibrosis trials vary by study and typically specify age range, disease stage or severity, prior treatment history, and specific diagnostic or laboratory parameters. Each listing on ClinicalMetric links to the full protocol on ClinicalTrials.gov, where inclusion and exclusion criteria are documented. Contact the sponsoring site's research coordinator directly to confirm your eligibility—your treating physician or specialist can also help identify the most appropriate trial based on your medical history and current treatment status.
Trial Phases
Phase 1
4
Phase 2
2
Top Sponsors
Vertex Pharmaceuticals Incorporated 2 trials
Children's Hospital Medical Center, Cincinnati 1 trial
University of Pennsylvania 1 trial
Cystetic Medicines, Inc. 1 trial
CHU de Reims 1 trial

Recruiting Clinical Trials

NCT04580368
Recruiting
Testing Drug Efficacy in Cystic Fibrosis Through N-of-1 Trials
Enrollment
50 pts
Location
United States
Sponsor
Children's Hospital Medical Ce...
View Trial →
NCT04731272 Phase 2
Recruiting
GLP-1 Agonist Therapy in Cystic Fibrosis-Related Glucose Intolerance
Enrollment
30 pts
Location
United States
Sponsor
University of Pennsylvania
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NCT05802264 Phase 1
Recruiting
Study to Assess Amphotericin B Cystetic for Inhalation (ABCI) Doses in Healthy Volunteers & People with Cystic Fibrosis
Enrollment
108 pts
Location
Australia, New Zeala...
Sponsor
Cystetic Medicines, Inc.
View Trial →
NCT07274631
Recruiting
A Cohort for Inflammatory Respiratory Diseases: From Phenotyping to Personalised Medicine
Enrollment
470 pts
Location
France
Sponsor
CHU de Reims
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NCT05504837 Phase 1
Recruiting
A Study Assessing KB407 for the Treatment of Cystic Fibrosis
Enrollment
20 pts
Location
United States
Sponsor
Krystal Biotech, Inc.
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NCT06457451
Recruiting
Impact of a Coordinated Dietetic-adapted Physical Activity Program on the Percentage of Lean Body Mass in Adults With Cystic Fibrosis Treated With Elexacaftor-Tezacaftor-Ivacaftor: Multicentre Randomised Controlled Trial
Enrollment
100 pts
Location
France
Sponsor
University Hospital, Tours
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NCT05099939
Recruiting
Identification of Dysglycemia With Continuous Glucose Monitoring to Assess Clinical Evolution in Cystic Fibrosis
Enrollment
121 pts
Location
Canada, France
Sponsor
Institut de Recherches Cliniqu...
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NCT06599892
Recruiting
CF Organization of Care in the Era of Highly Effective Modulator.
Enrollment
5,000 pts
Location
France
Sponsor
Hospices Civils de Lyon
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NCT06296394
Recruiting
Health Outcomes of Parents With Cystic Fibrosis-Aim 2
Enrollment
146 pts
Location
United States
Sponsor
University of Pittsburgh
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NCT06560463
Recruiting
Continuous Glucose Monitoring and OGTT Screen for Cystic Fibrosis Related Diabetes in Cystic Fibrosis
Enrollment
30 pts
Location
United States
Sponsor
Medical College of Wisconsin
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NCT06032273
Recruiting
Lung Transplant READY CF 2: CARING CF Ancillary RCT
Enrollment
132 pts
Location
United States
Sponsor
University of Washington
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NCT04530383 Phase 2
Recruiting
Metformin for People With CFRD on CFTR Modulator Therapy to Improve Ion Channel Function
Enrollment
30 pts
Location
United States
Sponsor
University of Kansas Medical C...
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NCT07283770 Phase 1
Recruiting
Dose Escalation Study Evaluating the Safety and Pharmacokinetics of VX-581 in Healthy Participants
Enrollment
136 pts
Location
United States
Sponsor
Vertex Pharmaceuticals Incorpo...
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NCT07437105 Phase 1
Recruiting
Dose Escalation Study Evaluating the Safety and Pharmacokinetics of VX-272 in Healthy Participants
Enrollment
128 pts
Location
United States
Sponsor
Vertex Pharmaceuticals Incorpo...
View Trial →

Related Conditions

cystic fibrosis related diabetes (2) pancreatic insufficiency (1) abnormal glucose tolerance (1) diabetes (1) chronic obstructive pulmonary disease (1) asthma (1) bronchiectasis (1) primary ciliary dyskinesia (1) parenthood status (1)
ClinicalMetric — Independent clinical trial intelligence platform. Not affiliated with NIH, ClinicalTrials.gov, the U.S. FDA, or any pharmaceutical company, hospital, or clinical research organization. Trial data is sourced from ClinicalTrials.gov for informational purposes only and does not constitute medical advice. Do not make any treatment, enrollment, or health decisions based solely on information found here — always consult a qualified healthcare professional. Full Disclaimer  ·  Last Reviewed: September 2026  ·  Data Methodology