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Medical Condition
myotonic dystrophy 1
Total Trials
2
Recruiting Now
2
Trial Phases
Phase 2
NCT03981575
Recruiting
Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
Enrollment
700 pts
Location
United States, Canad...
Sponsor
Virginia Commonwealth Universi...
NCT07220603 Phase 2
Recruiting
An Open-Label Extension Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1 (FREEDOM-OLE)
Enrollment
48 pts
Location
Canada
Sponsor
PepGen Inc