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Medical Condition

congenital myotonic dystrophy

Total Trials
1
Recruiting Now
1
Trial Phases
Phase 2, Phase 3
NCT05004129 Phase 2, Phase 3
Recruiting

Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy

Enrollment
76 pts
Location
United States, Austr...
Sponsor
AMO Pharma Limited
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