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Medical Condition
brain diseases metabolic inborn
Total Trials
2
Recruiting Now
2
Trial Phases
Phase 1
NCT02254863 Phase 1
Recruiting
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
Enrollment
40 pts
Location
United States
Sponsor
Joanne Kurtzberg, MD
NCT00237315
Recruiting
Longitudinal Study of Urea Cycle Disorders
Enrollment
1,500 pts
Location
United States, Canad...
Sponsor
Andrea Gropman