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Medical Condition

mucopolysaccharidosis ii

Total Trials
1
Recruiting Now
1
Trial Phases
Phase 1
NCT02254863 Phase 1
Recruiting

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Enrollment
40 pts
Location
United States
Sponsor
Joanne Kurtzberg, MD
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