← Back to Clinical Trials
Recruiting Phase 2 NCT07226453

Target Validation and Efficacy of Metformin in Patients With Posterior Fossa Group A (PFA) Ependymoma

Trial Parameters

Condition Posterior Fossa Ependymal Tumor
Sponsor University of California, San Francisco
Study Type INTERVENTIONAL
Phase Phase 2
Enrollment 30
Sex ALL
Min Age 1 Year
Max Age 39 Years
Start Date 2026-03-04
Completion 2028-04-30
Interventions
MetforminPlanned Surgical ResectionMagnetic Resonance Imaging (MRI)

Brief Summary

This is a multi-site study of the pharmacodynamic effects and efficacy of metformin in children and young adults with recurrent or progressive Posterior Fossa Group A (PFA) ependymoma.

Eligibility Criteria

Inclusion Criteria: 1. Participants must have recurrent or progressive posterior fossa A (PFA) ependymoma following surgery AND radiation treatment (RT). 2. Participants must have a diagnosis of PFA ependymoma either at initial diagnosis or at recurrence. Any number of previous recurrences are permissible provided the participant meets other enrollment criteria. 3. Participants must have adequate tumor tissue available from initial diagnosis or from pre- trial enrollment. Formalin-fixed paraffin-embedded (FFPE) material (1 full block) should be provided. If FFPE material is not available, 10 unstained slides with an accompanying hematoxylin and eosin (H\&E) report should be provided. Target Validation (TV) Phase: o Participants are candidates to undergo elective surgery for removal of all or a portion of their recurrent/progressive tumor. Efficacy Phase: * Participant must have measurable disease; this will be defined as lesions that can be accurately measured in two dimensions (longes

Related Trials