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Recruiting NCT04732910

NCT04732910 Modulate-CF: Cystic Fibrosis Transmembrane Regulator (CFTR) Biomarker Study to Evaluate the Rescue of Mutant CFTR in Patients With Cystic Fibrosis Treated With CFTR-modulators

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Clinical Trial Summary
NCT ID NCT04732910
Status Recruiting
Phase
Sponsor Charite University, Berlin, Germany
Condition Cystic Fibrosis
Study Type OBSERVATIONAL
Enrollment 500 participants
Start Date 2018-07-01
Primary Completion 2027-03-31

Eligibility & Interventions

Sex All sexes
Min Age 6 Months
Max Age N/A
Study Type OBSERVATIONAL
Interventions
Treatment with cystic fibrosis transmembrane regulator (CFTR) modualtors Ivacaftor, Lumacaftor-Ivacaftor, Tezacaftor-Ivacaftor, Elexacaftor-Tezacaftor-Ivacaftor, Vanzacaftor-Tezacaftor-Deutivacaftor

Eligibility Fast-Check

Enter your details for a quick preliminary check. This does not replace medical advice.

What to Expect as a Participant

This is an observational study. You will not receive an experimental treatment; researchers will collect data based on your existing condition or standard treatment.

This trial targets 500 participants in total. It began in 2018-07-01 with a primary completion date of 2027-03-31.

⚠ This information is for research awareness only. Always consult your physician before joining any clinical trial. Participation is voluntary and you may withdraw at any time.

Brief Summary

This observational study evaluates the effect of therapy with cystic fibrosis transmembrane regulator (CFTR) modulators on CFTR function measured by the CFTR biomarker intestinal current measurement (ICM), nasal potential difference (NPD) and sweat chloride in a post-approval setting in patients with cystic fibrosis (CF).

Eligibility Criteria

Inclusion Criteria: * Decision for cystic fibrosis (CF) transmembrane regulator (CFTR)-modulator therapy by the patient and the caring CF physician * Signed informed consent form (ICF) and, where appropriate, signed assent form. Exclusion Criteria: * Ongoing participation in an investigational drug study (including studies investigating lumacaftor, tezacaftor or ivacaftor)

Contact & Investigator

Central Contact

Simon Y Graeber, MD

✉ simon.graeber@charite.de

📞 +4930 450 566 587

Principal Investigator

Marcus A Mall, MD

PRINCIPAL INVESTIGATOR

Charite University, Berlin, Germany

Frequently Asked Questions

Who can join the NCT04732910 clinical trial?

This trial is open to participants of all sexes, aged 6 Months or older, studying Cystic Fibrosis. Full inclusion and exclusion criteria are listed in the Eligibility Criteria section. Always confirm your eligibility with the research team before applying.

Is NCT04732910 currently recruiting?

Yes, NCT04732910 is actively recruiting participants. Contact the research team at simon.graeber@charite.de for enrollment information.

Where is the NCT04732910 trial being conducted?

This trial is being conducted at Berlin, Germany, Giessen, Germany, Hanover, Germany, Heidelberg, Germany.

Who is sponsoring the NCT04732910 clinical trial?

NCT04732910 is sponsored by Charite University, Berlin, Germany. The principal investigator is Marcus A Mall, MD at Charite University, Berlin, Germany. The trial plans to enroll 500 participants.

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