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Recruiting Phase 3 NCT05682378

NCT05682378 Long-term Safety and Tolerability of Inclisiran in Participants With HeFH or HoFH Who Have Completed the Pediatric ORION-16, ORION-13, ORION-20, or ORION-19 Studies

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Clinical Trial Summary
NCT ID NCT05682378
Status Recruiting
Phase Phase 3
Sponsor Novartis Pharmaceuticals
Condition Heterozygous or Homozygous Familial Hypercholesterolemia
Study Type INTERVENTIONAL
Enrollment 195 participants
Start Date 2023-02-10
Primary Completion 2032-03-25

Eligibility & Interventions

Sex All sexes
Min Age 12 Years
Max Age 100 Years
Study Type INTERVENTIONAL
Interventions
Inclisiran

Eligibility Fast-Check

Enter your details for a quick preliminary check. This does not replace medical advice.

What to Expect as a Participant

You will actively receive the study intervention — which may be a drug, biologic, device, or procedure.

Phase 3 trials are large pivotal studies comparing the treatment to current standard of care or placebo. Your participation directly contributes to the evidence needed for regulatory approval.

This trial targets 195 participants in total. It began in 2023-02-10 with a primary completion date of 2032-03-25.

⚠ This information is for research awareness only. Always consult your physician before joining any clinical trial. Participation is voluntary and you may withdraw at any time.

Brief Summary

The purpose of this open-label, single arm, multicenter extension study is to evaluate the long-term safety and tolerability of inclisiran in participants with HeFH or HoFH who have completed the ORION-16 (CKJX839C12301), ORION-13 (CKJX839C12302), ORION-20 (CKJX839C12303) or ORION-19 (CKJX839C12304) studies.

Eligibility Criteria

Key inclusion: * Male and female participants with a diagnosis of HeFH or HoFH who completed the ORION-16, ORION-13, ORION-20 or ORION-19 studies * Per investigator's clinical judgment, participant derived benefit from treatment with inclisiran in the ORION-16, ORION-13, ORION-20 or ORION-19 studies Key exclusion: * Participants who in the feeder ORION-16, ORION-13, ORION-20, or ORION-19 studies either screen failed or permanently discontinued from the treatment/study for any reason or had serious safety or tolerability issues related to inclisiran treatment * Any uncontrolled or serious disease, or any medical, physical, or surgical condition, that may either interfere with participation in the clinical study or interpretation of clinical study results, and/or put the participant at significant risk

Contact & Investigator

Central Contact

Novartis Pharmaceuticals

✉ novartis.email@novartis.com

📞 1-888-669-6682

Principal Investigator

Novartis Pharmaceuticals

STUDY DIRECTOR

Novartis Pharmaceuticals

Frequently Asked Questions

Who can join the NCT05682378 clinical trial?

This trial is open to participants of all sexes, aged 12 Years or older, up to 100 Years, studying Heterozygous or Homozygous Familial Hypercholesterolemia. Full inclusion and exclusion criteria are listed in the Eligibility Criteria section. Always confirm your eligibility with the research team before applying.

What phase is the NCT05682378 trial and what does that mean for participants?

Phase 3 trials are large-scale studies comparing the new treatment to existing standards of care or a placebo. They provide the evidence needed for regulatory approval. This trial targets 195 participants.

Is NCT05682378 currently recruiting?

Yes, NCT05682378 is actively recruiting participants. Contact the research team at novartis.email@novartis.com for enrollment information.

Where is the NCT05682378 trial being conducted?

This trial is being conducted at Boca Raton, United States, New York, United States, Cincinnati, United States, Pittsburgh, United States and 11 additional locations.

Who is sponsoring the NCT05682378 clinical trial?

NCT05682378 is sponsored by Novartis Pharmaceuticals. The principal investigator is Novartis Pharmaceuticals at Novartis Pharmaceuticals. The trial plans to enroll 195 participants.

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ClinicalMetric — Independent clinical trial intelligence platform. Not affiliated with NIH, ClinicalTrials.gov, the U.S. FDA, or any pharmaceutical company, hospital, or clinical research organization. Trial data is sourced from ClinicalTrials.gov for informational purposes only and does not constitute medical advice. Do not make any treatment, enrollment, or health decisions based solely on information found here — always consult a qualified healthcare professional. Full Disclaimer  ·  Last Reviewed: September 2026  ·  Data Methodology