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Recruiting Phase 1, Phase 2 NCT05010122

NCT05010122 ASTX727, Venetoclax, and Gilteritinib for the Treatment of Newly Diagnosed, Relapsed or Refractory FLT3-Mutated Acute Myeloid Leukemia or High-Risk Myelodysplastic Syndrome

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Clinical Trial Summary
NCT ID NCT05010122
Status Recruiting
Phase Phase 1, Phase 2
Sponsor M.D. Anderson Cancer Center
Condition Acute Myeloid Leukemia
Study Type INTERVENTIONAL
Enrollment 42 participants
Start Date 2021-07-08
Primary Completion 2028-01-30

Trial Parameters

Condition Acute Myeloid Leukemia
Sponsor M.D. Anderson Cancer Center
Study Type INTERVENTIONAL
Phase Phase 1, Phase 2
Enrollment 42
Sex ALL
Min Age 18 Years
Max Age N/A
Start Date 2021-07-08
Completion 2028-01-30
Interventions
Decitabine and CedazuridineGilteritinibVenetoclax

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Brief Summary

This phase I/II trial studies the best dose of gilteritinib given together with ASTX727 and venetoclax and the effect of ASTX727, venetoclax, and gilteritinib in treating patients with FLT3-mutated acute myeloid leukemia that is newly diagnosed, has come back (relapsed) or does not respond to treatment (refractory) or high-risk myelodysplastic syndrome. Chemotherapy drugs, such as ASTX727, work in different ways to stop the growth of cancer cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Venetoclax may stop the growth of cancer cells by blocking Bcl-2, a protein needed for cancer cell survival. Gilteritinib may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth. Giving ASTX727, venetoclax, and gilteritinib may help to control the disease.

Eligibility Criteria

Inclusion Criteria: * Diagnosis: * Phase I cohort: Adults \>= 18 years with relapsed/refractory FLT3-mutated AML or myelodysplastic syndrome (MDS) that is intermediate-2 or high-risk by the International Prognostic Scoring System * Phase II cohort A: Adults \>= 18 years with newly diagnosed FLT3-mutated AML. Patients should meet the following criteria: * Confirmed newly diagnosed AML with FLT3 mutation * Ineligible for induction therapy defined as * Either age \>= 75 * Or 18-74 with at least one comorbidity (congestive heart failure \[CHF\] requiring therapy or ejection fraction \[EF\] =\< 50%, diffusion capacity of the lung for carbon monoxide \[DLCO\] =\< 65% or forced expiratory volume in 1 second \[FEV1\] =\< 65%, or Eastern Cooperative Oncology Group \[ECOG\] 2 or 3, or other significant co-morbidity precluding use of cytotoxic chemotherapy as approved by the principal investigator (PI) * Phase II cohort B: Adults \>= 18 years with relapsed/refractory FLT3-mutated AML or MDS that

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