SPONSOR
Johns Hopkins All Children's Hospital
Total Trials
2
Recruiting
2
Phases
Phase 2
Conditions studied: Hemoglobinopathy (Disorder)Severe Aplastic AnemiaBone Marrow Failure SyndromePrimary Immune Deficiency DisordersMetabolic Disease
NCT04356469 Phase 2
Recruiting
TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Non-Malignant Hematological Disorders in Children
Hemoglobinopathy (Disorder)
NCT04414046 Phase 2
Recruiting
TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Primary Immunodeficiency and Inherited Metabolic Disorders in Children
Primary Immune Deficiency Disorders