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Medical Condition

thalassemia

Total Trials
4
Recruiting Now
4
Trial Phases
EARLY_Phase 1, Phase 3

ClinicalMetric tracks all active clinical trials for thalassemia sourced from ClinicalTrials.gov. Research in this area spans early-phase safety investigations through large Phase 3 confirmatory trials, conducted by NIH-funded academic centers, independent investigators, and pharmaceutical sponsors worldwide. Each listing is updated daily as new studies open enrollment and existing ones reach capacity or complete follow-up.

Trial listings include the NCT identifier, current recruitment status, phase classification, primary and secondary endpoints, estimated enrollment size, participating countries, and direct links to the full protocol on ClinicalTrials.gov. Eligibility criteria — including age range, disease stage, and prior treatment requirements — are documented for every study to help patients and clinicians assess suitability before contacting a trial site.

Frequently Asked Questions — thalassemia Clinical Trials

How many clinical trials are currently recruiting for thalassemia?
ClinicalMetric currently tracks 4 actively recruiting clinical trials for thalassemia, sourced in real time from ClinicalTrials.gov. The total number of registered studies—including those not yet enrolling or in active follow-up—is 4. Trial availability changes daily as new studies open enrollment and existing ones reach capacity.
What trial phases are available for thalassemia?
thalassemia research spans Phase 1 (1 trial), Phase 3 (1 trial). Phase 1 studies evaluate safety and dosing in small groups, Phase 2 studies assess preliminary efficacy in 100–300 participants, and Phase 3 trials compare the new treatment against the standard of care in 300–3,000+ patients. Phase 4 post-approval studies monitor long-term outcomes in real-world populations.
How do I find out if I qualify for a thalassemia clinical trial?
Eligibility criteria for thalassemia trials vary by study and typically specify age range, disease stage or severity, prior treatment history, and specific diagnostic or laboratory parameters. Each listing on ClinicalMetric links to the full protocol on ClinicalTrials.gov, where inclusion and exclusion criteria are documented. Contact the sponsoring site's research coordinator directly to confirm your eligibility—your treating physician or specialist can also help identify the most appropriate trial based on your medical history and current treatment status.
Trial Phases
Phase 1
1
Phase 3
1
Top Sponsors
American Thrombosis and Hemostasis Network 1 trial
Shenzhen Hemogen 1 trial
Vertex Pharmaceuticals Incorporated 1 trial
Bristol-Myers Squibb 1 trial

Recruiting Clinical Trials

NCT04398628
Recruiting
ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
Enrollment
3,000 pts
Location
United States
Sponsor
American Thrombosis and Hemost...
View Trial →
NCT05745532 EARLY_Phase 1
Recruiting
Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients
Enrollment
10 pts
Location
China
Sponsor
Shenzhen Hemogen
View Trial →
NCT05477563 Phase 3
Recruiting
Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
Enrollment
26 pts
Location
United States, Germa...
Sponsor
Vertex Pharmaceuticals Incorpo...
View Trial →
NCT07215975
Recruiting
A Real-World Study to Evaluate Luspatercept in Adults With Transfusion-Dependent Beta-Thalassemia in the Middle East
Enrollment
200 pts
Location
Oman, Saudi Arabia
Sponsor
Bristol-Myers Squibb
View Trial →

Related Conditions

sickle cell disease (2) hematologic disorder (1) bleeding disorder (1) connective tissue disorder (1) hemophilia (1) thrombosis (1) von willebrand diseases (1) thrombophilia (1) rare bleeding disorder (1) platelet disorder (1) factor ix deficiency (1) factor viii deficiency (1)
ClinicalMetric — Independent clinical trial intelligence platform. Not affiliated with NIH, ClinicalTrials.gov, the U.S. FDA, or any pharmaceutical company, hospital, or clinical research organization. Trial data is sourced from ClinicalTrials.gov for informational purposes only and does not constitute medical advice. Do not make any treatment, enrollment, or health decisions based solely on information found here — always consult a qualified healthcare professional. Full Disclaimer  ·  Last Reviewed: April 2026  ·  Data Methodology