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Medical Condition

severe combined immunodeficiency x linked

Total Trials
2
Recruiting Now
2
Trial Phases
Phase 1, Phase 1, Phase 2
NCT03601286 Phase 1
Recruiting

Lentiviral Gene Therapy for X-linked Severe Combined Immunodeficiency

Enrollment
5 pts
Location
United Kingdom
Sponsor
Great Ormond Street Hospital f...
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NCT03311503 Phase 1, Phase 2
Recruiting

Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan Conditioning

Enrollment
12 pts
Location
United States
Sponsor
David Williams
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