← Browse by Condition
Medical Condition
gene therapy
Total Trials
4
Recruiting Now
4
Trial Phases
Phase 1, Phase 2
NCT07024524
Recruiting
Perceptual Evaluation and Rehabilitation System Development for Congenital Hearing Loss
Enrollment
210 pts
Location
China
Sponsor
Eye & ENT Hospital of Fudan Un...
NCT05991336
Recruiting
Growth and Development-related Outcomes in Children With Transfusion-dependent Beta-thalassemia After Gene Therapy
Enrollment
100 pts
Location
China
Sponsor
Institute of Hematology & Bloo...
NCT04728841
Recruiting
Gene Therapy for Chinese Hemophilia A
Enrollment
12 pts
Location
China
Sponsor
Institute of Hematology & Bloo...
NCT03311503 Phase 1, Phase 2
Recruiting
Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan Conditioning
Enrollment
12 pts
Location
United States
Sponsor
David Williams