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neuromuscular diseases nmd

Total Trials
6
Recruiting Now
6
Trial Phases
Phase 3

ClinicalMetric tracks all active clinical trials for neuromuscular diseases nmd sourced from ClinicalTrials.gov. Research in this area spans early-phase safety investigations through large Phase 3 confirmatory trials, conducted by NIH-funded academic centers, independent investigators, and pharmaceutical sponsors worldwide. Each listing is updated daily as new studies open enrollment and existing ones reach capacity or complete follow-up.

Trial listings include the NCT identifier, current recruitment status, phase classification, primary and secondary endpoints, estimated enrollment size, participating countries, and direct links to the full protocol on ClinicalTrials.gov. Eligibility criteria — including age range, disease stage, and prior treatment requirements — are documented for every study to help patients and clinicians assess suitability before contacting a trial site.

Frequently Asked Questions — neuromuscular diseases nmd Clinical Trials

How many clinical trials are currently recruiting for neuromuscular diseases nmd?
ClinicalMetric currently tracks 6 actively recruiting clinical trials for neuromuscular diseases nmd, sourced in real time from ClinicalTrials.gov. The total number of registered studies—including those not yet enrolling or in active follow-up—is 6. Trial availability changes daily as new studies open enrollment and existing ones reach capacity.
What trial phases are available for neuromuscular diseases nmd?
neuromuscular diseases nmd research spans Phase 3 (1 trial). Phase 1 studies evaluate safety and dosing in small groups, Phase 2 studies assess preliminary efficacy in 100–300 participants, and Phase 3 trials compare the new treatment against the standard of care in 300–3,000+ patients. Phase 4 post-approval studies monitor long-term outcomes in real-world populations.
How do I find out if I qualify for a neuromuscular diseases nmd clinical trial?
Eligibility criteria for neuromuscular diseases nmd trials vary by study and typically specify age range, disease stage or severity, prior treatment history, and specific diagnostic or laboratory parameters. Each listing on ClinicalMetric links to the full protocol on ClinicalTrials.gov, where inclusion and exclusion criteria are documented. Contact the sponsoring site's research coordinator directly to confirm your eligibility—your treating physician or specialist can also help identify the most appropriate trial based on your medical history and current treatment status.
Trial Phases
Phase 3
1
Top Sponsors
University of Missouri-Columbia 1 trial
University Hospital, Angers 1 trial
Seoul National University Hospital 1 trial
Intellia Therapeutics 1 trial
Rigshospitalet, Denmark 1 trial

Recruiting Clinical Trials

NCT07478172
Recruiting

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

Enrollment
50 pts
Location
United States
Sponsor
University of Missouri-Columbi...
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NCT07021638
Recruiting

EMMVIES : Walking Training at Home in VIrtual Reality for Children With Chronic Illnesses Impacting Physical Health

Enrollment
30 pts
Location
France
Sponsor
University Hospital, Angers
View Trial →
NCT06363357
Recruiting

The Effect of a Muscle-mimicking, Fabric-type Shoulder Orthosis on Functional Movements of the Upper Limb in Patients With Neuromuscular Disorder

Enrollment
30 pts
Location
South Korea
Sponsor
Seoul National University Hosp...
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NCT06672237 Phase 3
Recruiting

A Phase 3 Study of NTLA-2001 in ATTRv-PN

Enrollment
60 pts
Location
Argentina, Brazil, M...
Sponsor
Intellia Therapeutics
View Trial →
NCT07467187
Recruiting

Invasive Home Ventilation in Denmark

Enrollment
450 pts
Location
Denmark
Sponsor
Rigshospitalet, Denmark
View Trial →
NCT07477509
Recruiting

Northwestern Neuromuscular Disease Biorepository

Enrollment
2,500 pts
Location
United States
Sponsor
Northwestern University
View Trial →
ClinicalMetric — Independent clinical trial intelligence platform. Not affiliated with NIH, ClinicalTrials.gov, the U.S. FDA, or any pharmaceutical company, hospital, or clinical research organization. Trial data is sourced from ClinicalTrials.gov for informational purposes only and does not constitute medical advice. Do not make any treatment, enrollment, or health decisions based solely on information found here — always consult a qualified healthcare professional. Full Disclaimer  ·  Last Reviewed: April 2026  ·  Data Methodology