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Medical Condition
genetic diseases
Total Trials
2
Recruiting Now
2
Trial Phases
Various
ClinicalMetric tracks all active clinical trials for genetic diseases sourced from ClinicalTrials.gov. Each listing includes the NCT identifier, current recruitment status, phase, primary endpoints, sponsor, estimated enrollment, and participating countries — updated daily as new studies open and status changes.
- Recruiting trials currently enrolling participants, with eligibility criteria and age requirements
- Phase 1–4 studies from early safety trials to post-marketing surveillance
- NIH, pharmaceutical sponsor, and academic medical center studies worldwide
- AI-powered plain-language summary available for every trial listing
Top Sponsors
1 trial
1 trial
NCT06762002
Recruiting
Impaired Type I IFN Immunity Due to Autoantibodies or a Genetic Defect: a Prospective National Cohort
Enrollment
500 pts
Location
France
Sponsor
Institut National de la Santé ...
NCT06235580
Recruiting
Genotype-phenotype Characterization Study on Genetic Diseases With Immune and Neurological Dysfunctions
Enrollment
1,000 pts
Location
France
Sponsor
Imagine Institute