SPONSOR
Ionis Pharmaceuticals, Inc.
Total Trials
4
Recruiting
4
Phases
Phase 1, Phase 2, Phase 1, Phase 3
Conditions studied: Prion DiseaseMultiple System AtrophyHereditary Angioedema (HAE)Angelman Syndrome
Ionis Pharmaceuticals, Inc. is a clinical research sponsor with 4 registered studies on ClinicalTrials.gov, of which 4 are actively recruiting participants. Research covers conditions including Prion Disease, Multiple System Atrophy, Hereditary Angioedema (HAE), Angelman Syndrome.
The trial portfolio spans Phase 1, Phase 2, Phase 1, Phase 3 studies, reflecting a pipeline that may include early-stage safety evaluations, mid-stage efficacy assessments, and large-scale confirmatory trials. All studies listed here are sourced directly from ClinicalTrials.gov and updated daily.
Frequently Asked Questions — Ionis Pharmaceuticals, Inc.
How many clinical trials has Ionis Pharmaceuticals, Inc. sponsored?
ClinicalMetric currently tracks 4 clinical trials sponsored by Ionis Pharmaceuticals, Inc., of which 4 are actively recruiting participants. These trials cover conditions including Prion Disease, Multiple System Atrophy, Hereditary Angioedema (HAE). Trial counts are updated daily from ClinicalTrials.gov and reflect currently registered studies.
What therapeutic areas does Ionis Pharmaceuticals, Inc. research focus on?
Ionis Pharmaceuticals, Inc. clinical trials span Prion Disease, Multiple System Atrophy, Hereditary Angioedema (HAE), Angelman Syndrome. The research pipeline includes Phase 1, Phase 2, Phase 1, Phase 3 trials, reflecting work from early-stage safety evaluation through large-scale efficacy studies.
How do I participate in a Ionis Pharmaceuticals, Inc. clinical trial?
To participate in a Ionis Pharmaceuticals, Inc. trial, review the active studies listed on this page, check each trial's specific eligibility criteria on ClinicalTrials.gov, and contact the trial site directly—not the sponsor's headquarters. Trial sites are academic medical centers, hospitals, or specialized research clinics. Your physician can facilitate a referral. ClinicalMetric lists all Ionis Pharmaceuticals, Inc. trials with current recruitment status updated daily.
Clinical Trials by Ionis Pharmaceuticals, Inc.
NCT06153966 Phase 1, Phase 2
Recruiting
PrProfile: A Study to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ION717
Prion Disease
NCT04165486 Phase 1
Recruiting
Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of ION464 Administered to Adults With Multiple System Atrophy (HORIZON)
Multiple System Atrophy
NCT07298447 Phase 3
Recruiting
Donidalorsen Treatment in Children With Hereditary Angioedema
Hereditary Angioedema (HAE)
NCT05127226 Phase 1, Phase 2
Recruiting
HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
Angelman Syndrome
ClinicalMetric — Independent clinical trial intelligence platform. Not affiliated with NIH, ClinicalTrials.gov, the U.S. FDA, or any pharmaceutical company, hospital, or clinical research organization. Trial data is sourced from ClinicalTrials.gov for informational purposes only and does not constitute medical advice. Do not make any treatment, enrollment, or health decisions based solely on information found here — always consult a qualified healthcare professional. Full Disclaimer · Last Reviewed: July 2026 · Data Methodology