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SPONSOR

Ionis Pharmaceuticals, Inc.

Total Trials
3
Recruiting
3
Phases
Phase 1, Phase 2, Phase 1
Conditions studied: Pelizaeus-Merzbacher DiseasePrion DiseaseMultiple System Atrophy
NCT05659901
Recruiting

Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease

Pelizaeus-Merzbacher Disease
United States, France, Germany View Trial →
NCT06153966 Phase 1, Phase 2
Recruiting

PrProfile: A Study to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ION717

Prion Disease
United States, Australia, Canada View Trial →
NCT04165486 Phase 1
Recruiting

Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of ION464 Administered to Adults With Multiple System Atrophy (HORIZON)

Multiple System Atrophy
Austria, France, Germany View Trial →