SPONSOR
Genethon
Total Trials
3
Recruiting
3
Phases
Phase 2
NCT03466463
Recruiting
Gene Therapy for Severe Crigler Najjar Syndrome
Crigler-Najjar Syndrome
NCT06518005 Phase 2
Recruiting
Efficacy and Safety of GNT0003 Following Imlifidase Pre-treatment in Severe Crigler-Najjar Syndrome
Crigler-Najjar Syndrome
NCT03882827
Recruiting
Natural History of Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy