SPONSOR
BioMarin Pharmaceutical
Total Trials
3
Recruiting
3
Phases
Phase 2, Phase 3, Phase 4
BioMarin Pharmaceutical is a clinical research sponsor with 3 registered studies on ClinicalTrials.gov, of which 3 are actively recruiting participants. Research covers conditions including Achondroplasia, Phenylketonuria, Phenylketonuria, Maternal.
The trial portfolio spans Phase 2, Phase 3, Phase 4 studies, reflecting a pipeline that may include early-stage safety evaluations, mid-stage efficacy assessments, and large-scale confirmatory trials. All studies listed here are sourced directly from ClinicalTrials.gov and updated daily.
Frequently Asked Questions — BioMarin Pharmaceutical
How many clinical trials has BioMarin Pharmaceutical sponsored?
ClinicalMetric currently tracks 3 clinical trials sponsored by BioMarin Pharmaceutical, of which 3 are actively recruiting participants. These trials cover conditions including Achondroplasia, Phenylketonuria, Phenylketonuria, Maternal. Trial counts are updated daily from ClinicalTrials.gov and reflect currently registered studies.
What therapeutic areas does BioMarin Pharmaceutical research focus on?
BioMarin Pharmaceutical clinical trials span Achondroplasia, Phenylketonuria, Phenylketonuria, Maternal. The research pipeline includes Phase 2, Phase 3, Phase 4 trials, reflecting work from early-stage safety evaluation through large-scale efficacy studies.
How do I participate in a BioMarin Pharmaceutical clinical trial?
To participate in a BioMarin Pharmaceutical trial, review the active studies listed on this page, check each trial's specific eligibility criteria on ClinicalTrials.gov, and contact the trial site directly—not the sponsor's headquarters. Trial sites are academic medical centers, hospitals, or specialized research clinics. Your physician can facilitate a referral. ClinicalMetric lists all BioMarin Pharmaceutical trials with current recruitment status updated daily.
Clinical Trials by BioMarin Pharmaceutical
NCT07441876 Phase 2, Phase 3
Recruiting
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
Achondroplasia
NCT07477691 Phase 4
Recruiting
Immune Modulation During Palynziq® Treatment in Adults (IMPALA)
Phenylketonuria
NCT05579548
Recruiting
A Global, Multicenter Study to Assess Maternal, Fetal and Infant Outcomes of Exposure to Palynziq® (Pegvaliase) During Pregnancy and Breastfeeding
Phenylketonuria, Maternal
ClinicalMetric — Independent clinical trial intelligence platform. Not affiliated with NIH, ClinicalTrials.gov, the U.S. FDA, or any pharmaceutical company, hospital, or clinical research organization. Trial data is sourced from ClinicalTrials.gov for informational purposes only and does not constitute medical advice. Do not make any treatment, enrollment, or health decisions based solely on information found here — always consult a qualified healthcare professional. Full Disclaimer · Last Reviewed: April 2026 · Data Methodology