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Medical Condition

spastic paraplegia

Total Trials
1
Recruiting Now
1
Trial Phases
Phase 1, Phase 2
NCT05518188 Phase 1, Phase 2
Recruiting

Melpida: Recombinant Adeno-associated Virus (serotype 9) Encoding a Codon Optimized Human AP4M1 Transgene (hAP4M1opt)

Enrollment
4 pts
Location
United States
Sponsor
Elpida Therapeutics SPC
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