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Medical Condition

severe combined immunodeficiency due to rag1 deficiency

Total Trials
1
Recruiting Now
1
Trial Phases
Various
NCT04797260
Recruiting

Phase I/II Clinical Trial Stem Cell Gene Therapy in RAG1-Deficient SCID

Enrollment
10 pts
Location
Australia, Italy, Ne...
Sponsor
Leiden University Medical Cent...
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