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Medical Condition
propionic acidemia
Total Trials
2
Recruiting Now
2
Trial Phases
Various
NCT05040178
Recruiting
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
Enrollment
20 pts
Location
United States
Sponsor
RECORDATI GROUP
NCT02890342
Recruiting
Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
Enrollment
1,045 pts
Location
United States
Sponsor
National Human Genome Research...