← Browse by Condition
Medical Condition

persistent anemia

Total Trials
1
Recruiting Now
1
Trial Phases
Phase 1, Phase 2
NCT07187401 Phase 1, Phase 2
Recruiting

A First-in-Human Safety and Efficacy Study of ALN-CFB, a Small Interfering RNA (siRNA) Targeting Complement Factor B, in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria With Persistent Anemia on a C5 Inhibitor

Enrollment
24 pts
Location
Canada, South Korea,...
Sponsor
Regeneron Pharmaceuticals
View Trial →