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Medical Condition
paroxysmal nocturnal hemoglobinuria
Total Trials
2
Recruiting Now
2
Trial Phases
Phase 3, Phase 2
NCT07154745 Phase 3
Recruiting
A Study to Evaluate How Pozelimab + Cemdisiran Combination Therapy Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Whose Current Treatment is Not Working Efficiently
Enrollment
35 pts
Location
Italy, Poland, South...
Sponsor
Regeneron Pharmaceuticals
NCT06412497 Phase 2
Recruiting
MT2023-20: Hematopoietic Cell Transplant With Reduced Intensity Conditioning and Post-transplant Cyclophosphamide for Severe Aplastic Anemia and Other Forms of Acquired Bone Marrow Failure.
Enrollment
60 pts
Location
United States
Sponsor
Masonic Cancer Center, Univers...