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Medical Condition

paroxysmal nocturnal hemoglobinuria

Total Trials
4
Recruiting Now
4
Trial Phases
Phase 1, Phase 2, Phase 3

ClinicalMetric tracks all active clinical trials for paroxysmal nocturnal hemoglobinuria sourced from ClinicalTrials.gov. Research in this area spans early-phase safety investigations through large Phase 3 confirmatory trials, conducted by NIH-funded academic centers, independent investigators, and pharmaceutical sponsors worldwide. Each listing is updated daily as new studies open enrollment and existing ones reach capacity or complete follow-up.

Trial listings include the NCT identifier, current recruitment status, phase classification, primary and secondary endpoints, estimated enrollment size, participating countries, and direct links to the full protocol on ClinicalTrials.gov. Eligibility criteria — including age range, disease stage, and prior treatment requirements — are documented for every study to help patients and clinicians assess suitability before contacting a trial site.

Frequently Asked Questions — paroxysmal nocturnal hemoglobinuria Clinical Trials

How many clinical trials are currently recruiting for paroxysmal nocturnal hemoglobinuria?
ClinicalMetric currently tracks 4 actively recruiting clinical trials for paroxysmal nocturnal hemoglobinuria, sourced in real time from ClinicalTrials.gov. The total number of registered studies—including those not yet enrolling or in active follow-up—is 4. Trial availability changes daily as new studies open enrollment and existing ones reach capacity.
What trial phases are available for paroxysmal nocturnal hemoglobinuria?
paroxysmal nocturnal hemoglobinuria research spans Phase 1 (1 trial), Phase 2 (1 trial), Phase 3 (1 trial). Phase 1 studies evaluate safety and dosing in small groups, Phase 2 studies assess preliminary efficacy in 100–300 participants, and Phase 3 trials compare the new treatment against the standard of care in 300–3,000+ patients. Phase 4 post-approval studies monitor long-term outcomes in real-world populations.
How do I find out if I qualify for a paroxysmal nocturnal hemoglobinuria clinical trial?
Eligibility criteria for paroxysmal nocturnal hemoglobinuria trials vary by study and typically specify age range, disease stage or severity, prior treatment history, and specific diagnostic or laboratory parameters. Each listing on ClinicalMetric links to the full protocol on ClinicalTrials.gov, where inclusion and exclusion criteria are documented. Contact the sponsoring site's research coordinator directly to confirm your eligibility—your treating physician or specialist can also help identify the most appropriate trial based on your medical history and current treatment status.
Trial Phases
Phase 1
1
Phase 2
1
Phase 3
1
Top Sponsors
Jiangsu Hansoh Pharmaceutical Co., Ltd. 1 trial
Regeneron Pharmaceuticals 1 trial
International PNH Interest Group 1 trial
Novartis Pharmaceuticals 1 trial

Recruiting Clinical Trials

NCT07470762 Phase 1, Phase 2
Recruiting
Study of Safety and Efficacy of HS-10542 in Patients With Paroxysmal Nocturnal Hemoglobinuria
Enrollment
50 pts
Location
China
Sponsor
Jiangsu Hansoh Pharmaceutical ...
View Trial →
NCT07154745 Phase 3
Recruiting
A Study to Evaluate How Pozelimab + Cemdisiran Combination Therapy Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Whose Current Treatment is Not Working Efficiently
Enrollment
35 pts
Location
Brazil, Canada, Ital...
Sponsor
Regeneron Pharmaceuticals
View Trial →
NCT06524726
Recruiting
The International PNH Interest Group PNH Registry
Enrollment
2,000 pts
Location
United States
Sponsor
International PNH Interest Gro...
View Trial →
NCT07416162
Recruiting
A Study of Iptacopan in Korean Patients With Paroxysmal Nocturnal Hemoglobinuria or C3 Glomerulopathy
Enrollment
21 pts
Location
South Korea
Sponsor
Novartis Pharmaceuticals
View Trial →

Related Conditions

c3 glomerulopathy (1)
ClinicalMetric — Independent clinical trial intelligence platform. Not affiliated with NIH, ClinicalTrials.gov, the U.S. FDA, or any pharmaceutical company, hospital, or clinical research organization. Trial data is sourced from ClinicalTrials.gov for informational purposes only and does not constitute medical advice. Do not make any treatment, enrollment, or health decisions based solely on information found here — always consult a qualified healthcare professional. Full Disclaimer  ·  Last Reviewed: July 2026  ·  Data Methodology