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Medical Condition
ornithine transcarbamylase deficiency
Total Trials
3
Recruiting Now
3
Trial Phases
Phase 1, Phase 2, Phase 2
NCT06255782 Phase 1, Phase 2
Recruiting
An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency
Enrollment
8 pts
Location
United States, Austr...
Sponsor
iECURE, Inc.
NCT06488313 Phase 2
Recruiting
A Study to Evaluate the Pharmacodynamics and Safety of ARCT-810 in Participants With OTCD
Enrollment
9 pts
Location
United States
Sponsor
Arcturus Therapeutics, Inc.
NCT05092685 Phase 1, Phase 2
Recruiting
Halting Ornithine Transcarbamylase Deficiency With Recombinant AAV in ChildrEn
Enrollment
12 pts
Location
United Kingdom
Sponsor
University College, London