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Medical Condition

ngly1 deficiency

Total Trials
1
Recruiting Now
1
Trial Phases
Phase 1, Phase 2
NCT06199531 Phase 1, Phase 2
Recruiting

Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency

Enrollment
6 pts
Location
United States
Sponsor
Grace Science, LLC
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