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mucopolysaccharidosis type i

Total Trials
1
Recruiting Now
1
Trial Phases
Phase 1
NCT06519552 Phase 1
Recruiting

A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of JWK008 in Patients With Mucopolysaccharidosis Type I

Enrollment
6 pts
Location
China
Sponsor
West China Hospital
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