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Medical Condition
limb girdle muscular dystrophy
Total Trials
2
Recruiting Now
2
Trial Phases
Phase 1, Phase 2
NCT05230459 Phase 1, Phase 2
Recruiting
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)
Enrollment
10 pts
Location
United States
Sponsor
AskBio Inc
NCT01403402
Recruiting
Congenital Muscle Disease Study of Patient and Family Reported Medical Information
Enrollment
4,000 pts
Location
United States
Sponsor
Cure CMD