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glycogen storage disease type ia

Total Trials
2
Recruiting Now
2
Trial Phases
Various
NCT06636383
Recruiting

Glycogen Storage Disease Type Ia (GSDIa) Disease Monitoring Program

Enrollment
140 pts
Location
United States, Brazi...
Sponsor
Ultragenyx Pharmaceutical Inc
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NCT06843330
Recruiting

Accuracy of Lactate Meter in GSDIa

Enrollment
10 pts
Location
United States
Sponsor
Connecticut Children's Medical...
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