← Browse by Condition
Medical Condition
congenital myasthenic syndrome
Total Trials
2
Recruiting Now
2
Trial Phases
Phase 1
NCT06436742 Phase 1
Recruiting
A Phase 1b Study to Investigate Safety and Tolerability of ARGX-119 in Adult Participants With DOK7-Congenital Myasthenic Syndromes (CMS)
Enrollment
16 pts
Location
United States, Canad...
Sponsor
argenx
NCT01403402
Recruiting
Congenital Muscle Disease Study of Patient and Family Reported Medical Information
Enrollment
4,000 pts
Location
United States
Sponsor
Cure CMD