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Medical Condition

aromatic l amino acid decarboxylase aadc deficiency

Total Trials
1
Recruiting Now
1
Trial Phases
EARLY_Phase 1
NCT05765981 EARLY_Phase 1
Recruiting

An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.

Enrollment
6 pts
Location
China
Sponsor
Shanghai Jiao Tong University ...
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