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Medical Condition

alpha 1 antitrypsin deficiency

Total Trials
4
Recruiting Now
4
Trial Phases
Phase 3, Phase 1, Phase 2, Phase 1
NCT04204252 Phase 3
Recruiting

Phase III, Efficacy and Safety of "Kamada-AAT for Inhalation"

Enrollment
220 pts
Location
Belgium, Finland, Ir...
Sponsor
Kamada, Ltd.
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NCT06389877 Phase 1, Phase 2
Recruiting

A Study to Evaluate the Safety and Efficacy of BEAM-302 in Adult Patients With Alpha-1 Antitrypsin Deficiency (AATD)

Enrollment
106 pts
Location
United States, Austr...
Sponsor
Beam Therapeutics Inc.
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NCT06996756 Phase 1
Recruiting

Gene Therapy for Alpha 1- Antitrypsin Deficiency

Enrollment
16 pts
Location
United States
Sponsor
Weill Medical College of Corne...
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NCT07431112 Phase 1
Recruiting

A Study of AIR-001 in Adults With Alpha-1 Antitrypsin Deficiency (AATD)

Enrollment
54 pts
Location
Australia, United Ki...
Sponsor
AIRNA Corporation
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